Gene Therapies

NB: The discussion that follows does not consider germline gene therapy unnatural, ‘playing God’, or in-principle wrong. I subscribe to a continuity between artifice and nature, whereby anything created by humans is as much a natural product as humans themselves. Nothing is ‘going against’ some predetermined natural or divine plan…

Latest studies in precision medicine have shown progress toward managing human health and overall way of living. One such study comes from Oregon Science University College of Pharmacy, according to which genetically acquired blindness can now be treated through the assistance of lipid nanoparticles (LNPs). Researchers used LNPs and messenger…

Technology for early engagement can help pharma companies and payers co-create a vision of access, helping patients receive new treatments earlier, with manageable budget impact. Here’s how: In the past, the drugs and the deals needed to get them to market were relatively simple. But the pace of innovation is…

Multiple different drug modalities are used as therapeutics for the treatment of different diseases or illnesses. In this post, we will look at the different therapeutic modalities that exist in the pharma/biotech world. Drugs usually fall under 4 different types of modalities: 1) Small molecule 2) Biologics 3) Cell therapy…

Indiana University in Indianapolis, in the US, boasts a vector production facility that manufactures a critical component for gene therapy: engineered viruses specially designed to carry the code to correct faulty genes or to treat cancers. It is a highly specialised process that demands strict controls to ensure there is…

A Defense for Embryo Gene Design Genetic enhancement, or formally known as Embryo Gene Design (EGD), is an emerging and controversial technology in the medical field. EGD is an assisted reproductive technology where doctors take an embryo and alter its genes before implanting the embryo inside a mother. Although the…

Gene Therapy is the use of genetic materials to prevent or treat diseases. In Gene Therapy a new functional gene replaces the targeted gene to produce the correct functional protein. This therapeutic treatment may take place ‘In Vivo’ or ‘Ex Vivo’. Both Viral Vector and Non Viral Vector methods are…

A Fierce Pharma article explored the treatment paradigm in raising cancer and rare disease, sharing panellist viewpoints from the Fierce Biotech Next Gen virtual event in June 2022. …