Jessica LynninRareativesMiplyffa’s Approval Ignites Hope for the Niemann-Pick Type C (NPC) CommunityThis drug approval has been years in the making.Oct 3
Patrick TangyeI Know It’ll Get Better (But Right Now It’s Really Fucking Hard)Parenting a Baby With a Chronic ConditionDec 14, 202322
WagjihashUnveiling the Whittakers: A Family’s Extraordinary JourneyIn the heart of a small town secluded Appalachian town, located deep within the rolling hills, lived the enigmatic Whittaker family. For…Oct 20, 2023Oct 20, 2023
TheKnowHow_aeinTheKnowHow_aeFamilial HypercholesterolemiaDoes High Cholesterol Run in Your Family?Sep 25Sep 25
Dr. Nandadulal Sannigrahi, Ph.D ( Plant Biology)History is Good but Family History is Better than the Best“Study the past and you would define the future”- ConfuciusMay 8May 8
Jessica LynninRareativesMiplyffa’s Approval Ignites Hope for the Niemann-Pick Type C (NPC) CommunityThis drug approval has been years in the making.Oct 3
Patrick TangyeI Know It’ll Get Better (But Right Now It’s Really Fucking Hard)Parenting a Baby With a Chronic ConditionDec 14, 202322
WagjihashUnveiling the Whittakers: A Family’s Extraordinary JourneyIn the heart of a small town secluded Appalachian town, located deep within the rolling hills, lived the enigmatic Whittaker family. For…Oct 20, 2023
TheKnowHow_aeinTheKnowHow_aeFamilial HypercholesterolemiaDoes High Cholesterol Run in Your Family?Sep 25
Dr. Nandadulal Sannigrahi, Ph.D ( Plant Biology)History is Good but Family History is Better than the Best“Study the past and you would define the future”- ConfuciusMay 8
Dr. Seema Patel (PhD)inILLUMINATIONLet’s Talk About AcromegalyWhen growth hormones go berserkSep 2013
Will GreeneFrom Mila to millions: ultra-rare diseases, individualized medicines, and a promising new frontier…When Julia Vitarello’s once healthy, outgoing daughter, Mila, was diagnosed in 2016 with Batten disease, a rare and uniformly fatal genetic…Mar 13
Research OutreachBarth syndrome: A potential treatment for a rare diseaseBarth syndrome is a rare disorder in males caused by a variant of the gene TAFAZZIN. It affects the metabolism of the fat molecule…Aug 25