InE³ — Entertain Enlighten EmpowerbyWolfe KamomeBad Medicine and the Shadows of ScienceWhy the medicine you take could be bad for your healthJun 35
InWise & WellbyJohn Kruse MD, PhDPeople With Rare Conditions Deserve MedicationsBut are pharmaceutical companies abusing “Orphan Drug” rules?Dec 11, 202312
Congressional CommunitiesFeatured Article: Orphan Drug Act (March 15th, 2024)Congressional Communities is featuring one Congressional Research Service (CRS) article per day in effort to share with our readers the…Mar 15Mar 15
InPharm-OlambyRenee A ButlerImportance of Natural History Study to Rare Disease Drug DevelopmentRare disease drug development varies from the pathways seen in more established indications. The sample sizes are often extremely small…Dec 30, 2020Dec 30, 2020
InE³ — Entertain Enlighten EmpowerbyWolfe KamomeBad Medicine and the Shadows of ScienceWhy the medicine you take could be bad for your healthJun 35
InWise & WellbyJohn Kruse MD, PhDPeople With Rare Conditions Deserve MedicationsBut are pharmaceutical companies abusing “Orphan Drug” rules?Dec 11, 202312
Congressional CommunitiesFeatured Article: Orphan Drug Act (March 15th, 2024)Congressional Communities is featuring one Congressional Research Service (CRS) article per day in effort to share with our readers the…Mar 15
InPharm-OlambyRenee A ButlerImportance of Natural History Study to Rare Disease Drug DevelopmentRare disease drug development varies from the pathways seen in more established indications. The sample sizes are often extremely small…Dec 30, 2020
Andrea MantovaniWhat’s next for Orphan Drugs and ATMPs?More recently I had the opportunity to attend the World Orphan Drug Congress in Barcelona and I wanted to share my take aways and the…Apr 28, 2020
River D'Almeida, Ph.D‘Orphan drugs’ are ascendant. What will that mean for people with rare diseases?For most drugs, the path from the Petri dish to pharmacy shelves is paved with uncertainty. It’s a decade-long journey, with billions in…May 29, 2018