PinnedGeorge H. SimpsonCMT: It’s Worse Than You Think. But The End Just Might Be in SightIf you met someone with Charcot-Marie-Tooth (CMT), and they had a milder form, or were early in their progression, you’d think, “Well…Mar 24, 20221Mar 24, 20221
George H. SimpsonMeasuring Success by Empathy, not PowerI recently read a byliner by a professional writer musing about what she has learned about life as she aged. I started with great…Dec 19, 2023Dec 19, 2023
George H. SimpsonThe Job of Curing Charcot-Marie-Tooth Has Only Just BegunA few weeks ago, DTx Pharma announced that it had been acquired by Novartis. So what? Big pharma buys a lot of biotech companies that look…Aug 12, 2023Aug 12, 2023
George H. SimpsonEmotional Costs of Rare Diseases Are Far Greater than Treatment and Economic LosesThere is no single, globally accepted definition of what qualifies as a rare disease. Some definitions rely solely on the number of people…Apr 28, 2023Apr 28, 2023
George H. Simpson“I’m so filled with emotion…”Let’s say your daughter has a progressive, degenerative, neurological disease — like mine does. That means today is the best day of her…Oct 17, 2022Oct 17, 2022
George H. SimpsonAbout Being the Father of a Child with Charcot-Marie-ToothBeing the father of a child with CMT can be daunting especially since 1) you feel life-long guilt for having passed on the debilitating…Jul 26, 2022Jul 26, 2022
George H. SimpsonFive Reasons Why We Think the End of Charcot-Marie-Tooth is in SightNearly every instance of Charcot-Marie-Tooth (CMT) is caused by the mutation of a single gene and most genetic causes of CMT have been…Apr 11, 20221Apr 11, 20221
